This is exciting: the news story reports the first use of CRISPR to edit genes while still inside the human body. In this case, it is to treat Leber congenital amaurosis, a rare genetic disorder which causes blindness.
I hope that editing the genes for KD won't be too far behind!This message has been edited. Last edited by: Dan B,
Location: Brooklyn, NY
This is exciting.
Kennedy's Disease Association
PO Box 1105 Coarsegold CA 93614