|
Go | New | Find | Notify | Tools | Reply |
Registered: 08-02-2009 Posts: 204 | The news media in the U.K. have reported that the first child there was treated with a new drug called Zolgensma, which is a gene-editing therapy that corrects the faulty gene causing Spinal Muscular Atrophy or SMA. Obviously this is not the same as SBMA or Kennedy's Disease, but still, the notion that gene editing is being used to cure a neurological disorder is very encouraging. Here's the article. https://www.pmlive.com/pharma_...py_zolgensma_1371002 |
Powered by Social Strata |
Please Wait. Your request is being processed... |
Kennedy's Disease Association
1445 Woodmont Ln NW #1805 GA 30318
Tel: 1-855-532-7762
Email: info@kennedysdisease.org