Home Login/Join My Space Help Members Forums Search Today's Active Topics New Since Last Visit
Kennedys Disease Association Homepage    Kennedys Disease Community    Forums  Hop To Forum Categories  General Discussion  Hop To Forums  Medications and Therapies    News about drug Zolgensma used to treat SMA

Moderators: Bruce, SusanneW
Go
New
Find
Notify
Tools
Reply
  
News about drug Zolgensma used to treat SMA
 Login/Join
 
Registered: 08-02-2009
Posts: 204
posted   Reply With QuoteReport This Post  
The news media in the U.K. have reported that the first child there was treated with a new drug called Zolgensma, which is a gene-editing therapy that corrects the faulty gene causing Spinal Muscular Atrophy or SMA.

Obviously this is not the same as SBMA or Kennedy's Disease, but still, the notion that gene editing is being used to cure a neurological disorder is very encouraging.

Here's the article.

https://www.pmlive.com/pharma_...py_zolgensma_1371002
  Powered by Social Strata  
 

Kennedys Disease Association Homepage    Kennedys Disease Community    Forums  Hop To Forum Categories  General Discussion  Hop To Forums  Medications and Therapies    News about drug Zolgensma used to treat SMA

Kennedy's Disease Association
PO Box 1105 Coarsegold CA 93614
Tel: 1-855-532-7762
Email: info@kennedysdisease.org